‘Too Rare to Care’? A New Center for Rare Diseases Hopes to Change That

A new nonprofit wants to streamline gene therapy for diseases often avoided by pharmaceutical companies — making treatment ...
STAT

Broad Institute, partners unveil new initiative to develop gene therapies for rare diseases

The Broad Institute, Boston Children’s Hospital, and Maine’s Jackson Laboratory announced a collaboration to develop rare ...

Broad Institute, Boston Children's Hospital, and The Jackson Laboratory launch the Center for Therapeutic Genetics, a non-profit effort to develop genetic medicines for rare ...

Broad Institute, Boston Children's Hospital, and The Jackson Laboratory today announced the Center for Therapeutic Genetics (CTG), a collaboration that will develop genetic medicines and treat ...

This Biotech Lets Rare-Disease Families Invest In Its Gene Therapy

Rare-disease families can now invest in Mahzi Therapeutics' gene therapy, giving patients a financial stake in developing ...

Chan Zuckerberg Initiative's Biohub to open new rare disease funding round

Chan Zuckerberg Initiative's Biohub will offer new grants to the rare disease community while expanding its AI drug repurposing partnership with Every Cure.
STAT

The quest to save Grace — and clear the way for rare disease patients everywhere

Mast and Herper have covered rare disease issues for a combined three decades. As part of the reporting, Mast spent two days ...
India Today on MSN

Anthropic is paying researchers up to $50,000 in AI credits to find rare diseases

Anthropic is betting that AI can make a difference in rare disease research. It has launched a new programme through which it ...

Plasma exchange could expand treatment options for rare disease that threatens vision

Plasma exchange can help treat people with a rare inflammatory disease that can cause blindness, according to a systematic ...

Anthropic offers up to $50,000 in AI credits to help researchers find rare disease treatments

Anthropic has launched a new initiative within its AI for Science program, offering selected researchers and early-stage ...

Risk of rare genetic diseases is higher for some Scottish Travellers, study says

Scientists from the University of Edinburgh carried out the first major genetic study of the community.

Inhibrx Biosciences: The Rare Disease Launch Is Only The Opening Act

Inhibrx is transitioning from a platform to a clinical-stage biotech, with ozekibart and INBRX-106 as key value drivers.