The US Food and Drug Administration has approved Acadia Pharmaceuticals’ Daybue Stix (trofinetide), a dye and ...

Trofinetide is a synthetic analog of the N-terminal tripeptide of insulin-like growth factor 1. The mechanism by which ...

After her daughter A'Laiya was injured at school, Latarsher Allen shares harrowing details and her ongoing fight for policy changes.

Neuren Pharmaceuticals Limited ( ($AU:NEU) ) has provided an update. Neuren Pharmaceuticals announced that its partner, Acadia Pharmaceuticals, ...

Daybue Stix, a strawberry-flavored trofinetide powder mixable with water-based liquids, gains FDA approval for Rett syndrome treatment.

An expert discusses the current treatment landscape of Rett syndrome including the goals of treatment and implications for utilization management strategies with the disease. David Lieberman, MD, PhD: ...

In commemoration of Rett syndrome awareness month this October, Acadia Pharmaceuticals is launching an awareness campaign to shine a light on patients' journeys and show that each person living with ...

Ella Frank, 15, has battled lifetime to challenges from rare neurological disorder. Her parents must replace special van to keep treatment on track.

David Lieberman, MD, PhD, reviews the economic burden and long-term complications of Rett syndrome as well as highlights the unmet needs for patients. David Lieberman, MD, PhD: Some long-term ...

Rare genetic disorder shuts off motor skills; mental acuity may still be there. May 9, 2012— -- For the first year of life, Chelsea Coenraads was a perfectly normal child, playing peek-a-boo and ...

What is Rett syndrome and why does it affect only girls? Rett syndrome is a rare neurological disorder that causes victims to regress intellectually, gradually robbing their ability to think and move.